BeursBonobo schreef op 2 november 2017 09:18:
Misschien interessant om op ter merken / dicussieren
1)
Friday 3 November
Oral session W18: Innovative approaches to CF therapies, 2:20 -2:30 am
Corina Balut - abstract #198, DEVELOPMENT AND CHARACTERIZATION OF NEXT-GENERATION CORRECTORS AS PART OF A TRIPLE CF THERAPY
Geeft wellicht het plaatje weer over hoe goede de correctors van GLPG zijn (characterization?)
2) Poster #36
SAFETY, TOLERABILITY AND PHARMACOKINETICS OF A NOVEL CFTR POTENTIATOR GLPG3067 IN HEALTHY VOLUNTEERS, accompanied by Magdalena Petkova
Geeft weer hoe goed de potentiator is van GLPG?
3)Poster #259
GLPG1837 IN SUBJECTS WITH CYSTIC FIBROSIS AND THE S1251N OR G551D MUTATION: RESULTS FROM PHASE 2A STUDIES (SAPHIRA 1 AND 2), accompanied by Katja Conrath
Poster #263
PHARMACOKINETICS AND SAFETY OF A NOVEL CFTR CORRECTOR MOLECULE GLPG2222 IN HEALTHY SUBJECTS AND IN SUBJECTS WITH CYSTIC FIBROSIS: RESULTS FROM TWO PHASE I STUDIES, accompanied by Olivier van de Steen
Studieresultaten! (Waren deze al bekend?)
4) Poster #167
TESTING EFFICACY OF NOVEL CORRECTORS AND POTENTIATORS IN RESCUING A RARE CYSTIC FIBROSIS MUTATION BY FUNCTIONAL SCREENING OF A CRISPR/CAS9-ENGINEERED BRONCHIAL CELL LINE, accompanied by Paul Eckford
Klinkt als iets nieuws?
5) Poster #27
MUTATIONS IN THE SECOND CYTOPLASMIC LOOP OF CFTR SUGGEST DISTINCT MODE OF ACTION BETWEEN POTENTIATORS VX-770 AND GLPG1837, accompanied by Marjolein Mijnders
Directe vergelijking met VERTEX potentiator? (Zou je niet 123 zelf laten zien je zelf niet beter bent?)